Advancing Strategies for Preclinical to Clinical Development Success in mRNA-Based Therapeutics for Rare Diseases
11.30 Discovery to Clinic: mRNA as a Potential Treatment for Rare Disease
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Patrick Finn, VP – Rare Disease Research & Preclinical Development, Moderna
12.00 Clinical Immunogenicity of LNP-Encapsulated RNA Therapeutics & Impact on Drug Development
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Tao Niu, Associate Director – Clinical & Quantitative Pharmacology, Vertex
Pharmaceuticals
12.30 Preclinical Study Considerations for mRNA-Based Therapeutics to Initiate Successful Clinical Studies
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Arunan Kaliyaperumal, VP – Preclinical Biology, ReCode Therapeutics