Simone Spuler

Company: Max Delbrück Center for Molecular Medicine & Charité – Universitätsmedizin Berlin; MyoPax

Job title: Professor; Co-founder

Seminars:

mRNA-Mediated Delivery of CRISPR/Cas9 Tools to Human Muscle Stem Cells in Muscular Dystrophy 10:00 am

Monogenic muscular dystrophies Highly effective and safe mutation corrections by base editing and by classical Cas9 First-in-human clinical trial in advanced planning (bASKet-trial)Read more

day: Pre-Conference Focus Day

Panel Discussion – Delving into Innovative mRNA Technologies for Gene Editing for Powerful mRNA-Based Treatments 10:30 am

Leveraging the developments of mRNA-based gene editing to outline the roadmap for future therapeutic avenues Discussing key technologies and their relative advantages and drawbacks for gene deliveryRead more

day: Pre-Conference Focus Day